[{"id":"ef9f9bd0-273f-42be-ab92-31c003721bbd","acronym":"","url":"https://clinicaltrials.gov/study/NCT01861106","created_at":"2021-01-18T08:19:16.098Z","updated_at":"2025-02-25T12:26:02.331Z","phase":"Phase 2","brief_title":"Allogeneic Hematopoietic Stem Cell Transplant for GATA2 Mutations","source_id_and_acronym":"NCT01861106","lead_sponsor":"National Cancer Institute (NCI)","biomarkers":" GATA2","pipe":" | ","alterations":" GATA2 mutation","tags":["GATA2"," \u003cb class=\"violet\"\u003e|\u003c/b\u003e GATA2 mutation"," \u003cb class=\"violet\"\u003e|\u003c/b\u003e cyclophosphamide • fludarabine IV • busulfan • cyclophosphamide intravenous"],"overall_status":"Recruiting","enrollment":" Enrollment 144","initiation":"Initiation: 07/24/2013","start_date":" 07/24/2013","primary_txt":" Primary completion: 12/31/2027","primary_completion_date":" 12/31/2027","study_txt":" Completion: 12/31/2028","study_completion_date":" 12/31/2028","last_update_posted":"2025-02-24"},{"id":"421063e1-092c-4069-8aae-f069c4e61471","acronym":"","url":"https://clinicaltrials.gov/study/NCT01174108","created_at":"2021-01-18T04:41:02.291Z","updated_at":"2025-02-25T15:25:06.019Z","phase":"Phase 2","brief_title":"Allogeneic Hematopoietic Stem Cell Transplantation for Severe Aplastic Anemia and Other Bone Marrow Failure Syndromes Using G-CSF Mobilized CD34+ Selected Hematopoietic Precursor Cells Co-Infused With a Reduced Dose of Non-Mobilized Donor T-cells","source_id_and_acronym":"NCT01174108","lead_sponsor":"National Heart, Lung, and Blood Institute (NHLBI)","biomarkers":" TERT • GATA2","pipe":" | ","alterations":" TERT mutation • GATA2 mutation","tags":["TERT • GATA2"," \u003cb class=\"violet\"\u003e|\u003c/b\u003e TERT mutation • GATA2 mutation"],"overall_status":"Recruiting","enrollment":" Enrollment 120","initiation":"Initiation: 12/10/2010","start_date":" 12/10/2010","primary_txt":" Primary completion: 12/30/2025","primary_completion_date":" 12/30/2025","study_txt":" Completion: 06/30/2028","study_completion_date":" 06/30/2028","last_update_posted":"2025-02-11"},{"id":"9aebc143-6452-41c7-82b0-b0dff845f7ed","acronym":"MORE","url":"https://clinicaltrials.gov/study/NCT05796570","created_at":"2023-04-03T14:03:12.035Z","updated_at":"2024-07-02T16:35:50.039Z","phase":"Phase 2","brief_title":"A Pilot Study to Evaluate the Feasibility of Post-Hematopoietic Stem Cell Transplant Prophylaxis With Decitabine Combined With Filgrastim for Children and Young Adults With AML, MDS and Related Myeloid Malignancies","source_id_and_acronym":"NCT05796570 - MORE","lead_sponsor":"Franziska Wachter","biomarkers":" RUNX1 • ETV6 • DDX41 • GATA2 • ANKRD26","pipe":" | ","alterations":" RUNX1 mutation • DDX41 mutation • GATA2 mutation • ETV6 mutation","tags":["RUNX1 • ETV6 • DDX41 • GATA2 • ANKRD26"," \u003cb class=\"violet\"\u003e|\u003c/b\u003e RUNX1 mutation • DDX41 mutation • GATA2 mutation • ETV6 mutation"," \u003cb class=\"violet\"\u003e|\u003c/b\u003e decitabine • Neupogen (filgrastim)"],"overall_status":"Recruiting","enrollment":" Enrollment 37","initiation":"Initiation: 04/19/2023","start_date":" 04/19/2023","primary_txt":" Primary completion: 09/01/2026","primary_completion_date":" 09/01/2026","study_txt":" Completion: 09/01/2029","study_completion_date":" 09/01/2029","last_update_posted":"2023-04-20"},{"id":"eb38da98-388d-47b0-b07d-0f89209aaf70","acronym":"","url":"https://clinicaltrials.gov/study/NCT00923364","created_at":"2021-01-18T03:34:28.566Z","updated_at":"2024-07-02T16:36:48.730Z","phase":"Phase 2","brief_title":"Pilot and Feasibility Study of Reduced-Intensity Hematopoietic Stem Cell Transplant for MonoMAC","source_id_and_acronym":"NCT00923364","lead_sponsor":"National Cancer Institute (NCI)","biomarkers":" HLA-DRB1 • CD34 • HLA-DQB1 • GATA2 • HLA-B • HLA-C","pipe":" | ","alterations":" GATA2 mutation","tags":["HLA-DRB1 • CD34 • HLA-DQB1 • GATA2 • HLA-B • HLA-C"," \u003cb class=\"violet\"\u003e|\u003c/b\u003e GATA2 mutation"," \u003cb class=\"violet\"\u003e|\u003c/b\u003e cyclophosphamide • fludarabine IV • cyclophosphamide intravenous"],"overall_status":"Completed","enrollment":" Enrollment 19","initiation":"Initiation: 05/07/2009","start_date":" 05/07/2009","primary_txt":" Primary completion: 06/12/2014","primary_completion_date":" 06/12/2014","study_txt":" Completion: 02/26/2017","study_completion_date":" 02/26/2017","last_update_posted":"2020-03-12"}]